Economic evaluation in the context of rare diseases: is it possible?

Detalhes bibliográficos
Autor(a) principal: Everton Nunes da Silva
Data de Publicação: 2015
Outros Autores: Tanara Rosângela Vieira Sousa
Tipo de documento: Artigo
Idioma: eng
por
Título da fonte: Cadernos de Saúde Pública
Texto Completo: https://cadernos.ensp.fiocruz.br/ojs/index.php/csp/article/view/5985
Resumo: This study analyzes the available evidence on the adequacy of economic evaluation for decision-making on the incorporation or exclusion of technologies for rare diseases. The authors conducted a structured literature review in MEDLINE via PubMed, CRD, LILACS, SciELO, and Google Scholar (gray literature). Economic evaluation studies had their origins in Welfare Economics, in which individuals maximize their utilities based on allocative efficiency. There is no widely accepted criterion in the literature to weigh the expected utilities, in the sense of assigning more weight to individuals with greater health needs. Thus, economic evaluation studies do not usually weigh utilities asymmetrically (that is, everyone is treated equally, which in Brazil is also a Constitutional principle). Healthcare systems have ratified the use of economic evaluation as the main tool to assist decision-making. However, this approach does not rule out the use of other methodologies to complement cost-effectiveness studies, such as Person Trade-Off and Rule of Rescue.
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spelling Economic evaluation in the context of rare diseases: is it possible?Avaliação econômica no âmbito das doenças raras: isto é possível?Cost-Effectiveness EvaluationRare DiseasesHealth EconomicsAvaliação de Custo-EfetividadeDoenças RarasEconomia da SaúdeThis study analyzes the available evidence on the adequacy of economic evaluation for decision-making on the incorporation or exclusion of technologies for rare diseases. The authors conducted a structured literature review in MEDLINE via PubMed, CRD, LILACS, SciELO, and Google Scholar (gray literature). Economic evaluation studies had their origins in Welfare Economics, in which individuals maximize their utilities based on allocative efficiency. There is no widely accepted criterion in the literature to weigh the expected utilities, in the sense of assigning more weight to individuals with greater health needs. Thus, economic evaluation studies do not usually weigh utilities asymmetrically (that is, everyone is treated equally, which in Brazil is also a Constitutional principle). Healthcare systems have ratified the use of economic evaluation as the main tool to assist decision-making. However, this approach does not rule out the use of other methodologies to complement cost-effectiveness studies, such as Person Trade-Off and Rule of Rescue.El objetivo fue sistematizar las evidencias disponibles sobre la pertinencia de utilizar la evaluación económica para la incorporación/exclusión de tecnología en enfermedades raras. Se realizó una revisión sistemática de la literatura en MEDLINE vía PubMed, CRD, LILACS, SciELO y Google Académico (literatura gris). Los estudios de evaluación económica se originan de la Economía del Bienestar, en la que los individuos maximizan sus utilidades, basándose en la eficiencia de asignación. No existe un criterio ampliamente aceptado para examinar las utilidades, a fin de dar más peso a los individuos con mayores necesidades. Generalmente, los estudios no equilibran asimétricamente las utilidades, todas son consideradas iguales, lo que en Brasil es también un principio constitucional. Los sistemas de salud han ratificado el uso de la evaluación económica como la principal herramienta para ayudar en la toma de decisiones. Sin embargo, este abordaje no excluye el uso de otras metodologías complementarias a los estudios de coste-efectividad, como la técnica de compensación personal o la regla del rescate.O objetivo deste estudo foi analisar as evidências disponíveis sobre a adequação do uso de avaliação econômica sobre incorporação/exclusão de tecnologias para doenças raras. Foi realizada uma revisão estruturada da literatura, nas bases MEDLINE, via PubMed, CRD, LILACS, SciELO e Google Acadêmico (literatura cinzenta). Os estudos de avaliação econômica têm origem na Economia do Bem-Estar, na qual os indivíduos maximizam suas utilidades, fundamentando-se na eficiência alocativa. Não há um critério amplamente aceito para ponderar as utilidades esperadas, no sentido de dar mais peso aos indivíduos com maiores necessidades em saúde. Geralmente não se ponderam assimetricamente as utilidades; todas são tratadas de forma igualitária, que, no caso brasileiro, também é um princípio constitucional. Os sistemas de saúde têm ratificado o uso de avaliação econômica como principal instrumento para auxiliar na tomada de decisão. No entanto, essa postura não exclui o uso de outras metodologias complementares aos estudos de custo-efetividade, como Person Trade-Off e regra de resgate.Reports in Public HealthCadernos de Saúde Pública2015-03-01info:eu-repo/semantics/articleinfo:eu-repo/semantics/publishedVersiontext/htmltext/htmlapplication/pdfapplication/pdfhttps://cadernos.ensp.fiocruz.br/ojs/index.php/csp/article/view/5985Reports in Public Health; Vol. 31 No. 3 (2015): MarchCadernos de Saúde Pública; v. 31 n. 3 (2015): Março1678-44640102-311Xreponame:Cadernos de Saúde Públicainstname:Fundação Oswaldo Cruz (FIOCRUZ)instacron:FIOCRUZengporhttps://cadernos.ensp.fiocruz.br/ojs/index.php/csp/article/view/5985/12566https://cadernos.ensp.fiocruz.br/ojs/index.php/csp/article/view/5985/12567https://cadernos.ensp.fiocruz.br/ojs/index.php/csp/article/view/5985/12568https://cadernos.ensp.fiocruz.br/ojs/index.php/csp/article/view/5985/12569Everton Nunes da SilvaTanara Rosângela Vieira Sousainfo:eu-repo/semantics/openAccess2024-03-06T15:29:02Zoai:ojs.teste-cadernos.ensp.fiocruz.br:article/5985Revistahttps://cadernos.ensp.fiocruz.br/ojs/index.php/csphttps://cadernos.ensp.fiocruz.br/ojs/index.php/csp/oaicadernos@ensp.fiocruz.br||cadernos@ensp.fiocruz.br1678-44640102-311Xopendoar:2024-03-06T13:06:50.007352Cadernos de Saúde Pública - Fundação Oswaldo Cruz (FIOCRUZ)true
dc.title.none.fl_str_mv Economic evaluation in the context of rare diseases: is it possible?
Avaliação econômica no âmbito das doenças raras: isto é possível?
title Economic evaluation in the context of rare diseases: is it possible?
spellingShingle Economic evaluation in the context of rare diseases: is it possible?
Everton Nunes da Silva
Cost-Effectiveness Evaluation
Rare Diseases
Health Economics
Avaliação de Custo-Efetividade
Doenças Raras
Economia da Saúde
title_short Economic evaluation in the context of rare diseases: is it possible?
title_full Economic evaluation in the context of rare diseases: is it possible?
title_fullStr Economic evaluation in the context of rare diseases: is it possible?
title_full_unstemmed Economic evaluation in the context of rare diseases: is it possible?
title_sort Economic evaluation in the context of rare diseases: is it possible?
author Everton Nunes da Silva
author_facet Everton Nunes da Silva
Tanara Rosângela Vieira Sousa
author_role author
author2 Tanara Rosângela Vieira Sousa
author2_role author
dc.contributor.author.fl_str_mv Everton Nunes da Silva
Tanara Rosângela Vieira Sousa
dc.subject.por.fl_str_mv Cost-Effectiveness Evaluation
Rare Diseases
Health Economics
Avaliação de Custo-Efetividade
Doenças Raras
Economia da Saúde
topic Cost-Effectiveness Evaluation
Rare Diseases
Health Economics
Avaliação de Custo-Efetividade
Doenças Raras
Economia da Saúde
description This study analyzes the available evidence on the adequacy of economic evaluation for decision-making on the incorporation or exclusion of technologies for rare diseases. The authors conducted a structured literature review in MEDLINE via PubMed, CRD, LILACS, SciELO, and Google Scholar (gray literature). Economic evaluation studies had their origins in Welfare Economics, in which individuals maximize their utilities based on allocative efficiency. There is no widely accepted criterion in the literature to weigh the expected utilities, in the sense of assigning more weight to individuals with greater health needs. Thus, economic evaluation studies do not usually weigh utilities asymmetrically (that is, everyone is treated equally, which in Brazil is also a Constitutional principle). Healthcare systems have ratified the use of economic evaluation as the main tool to assist decision-making. However, this approach does not rule out the use of other methodologies to complement cost-effectiveness studies, such as Person Trade-Off and Rule of Rescue.
publishDate 2015
dc.date.none.fl_str_mv 2015-03-01
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dc.identifier.uri.fl_str_mv https://cadernos.ensp.fiocruz.br/ojs/index.php/csp/article/view/5985
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dc.language.iso.fl_str_mv eng
por
language eng
por
dc.relation.none.fl_str_mv https://cadernos.ensp.fiocruz.br/ojs/index.php/csp/article/view/5985/12566
https://cadernos.ensp.fiocruz.br/ojs/index.php/csp/article/view/5985/12567
https://cadernos.ensp.fiocruz.br/ojs/index.php/csp/article/view/5985/12568
https://cadernos.ensp.fiocruz.br/ojs/index.php/csp/article/view/5985/12569
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dc.publisher.none.fl_str_mv Reports in Public Health
Cadernos de Saúde Pública
publisher.none.fl_str_mv Reports in Public Health
Cadernos de Saúde Pública
dc.source.none.fl_str_mv Reports in Public Health; Vol. 31 No. 3 (2015): March
Cadernos de Saúde Pública; v. 31 n. 3 (2015): Março
1678-4464
0102-311X
reponame:Cadernos de Saúde Pública
instname:Fundação Oswaldo Cruz (FIOCRUZ)
instacron:FIOCRUZ
instname_str Fundação Oswaldo Cruz (FIOCRUZ)
instacron_str FIOCRUZ
institution FIOCRUZ
reponame_str Cadernos de Saúde Pública
collection Cadernos de Saúde Pública
repository.name.fl_str_mv Cadernos de Saúde Pública - Fundação Oswaldo Cruz (FIOCRUZ)
repository.mail.fl_str_mv cadernos@ensp.fiocruz.br||cadernos@ensp.fiocruz.br
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